Fierce Pharma
Fierce Biotech
Fierce Healthcare
Fierce Life Sciences Events
Advertise
About Us
Pharma
Vaccines
Asia
Cell & Gene Therapy
Drug Delivery
Executives
Manufacturing
Facilities
Recalls
Warning Letters
Marketing
Special Reports
Fierce 50
Special Report
Awards Gala
Trending
Oncology
Supply Chain
AI and Machine Learning
Awards
Outsourcing Awards
Innovation Awards
Pharma Marketing Awards
Resources
Podcasts
Fierce Events
Industry Events
Webinars
Whitepapers
Survey
Events
Subscribe
Subscribe
Pharma
Vaccines
Asia
Cell & Gene Therapy
Drug Delivery
Executives
Manufacturing
Facilities
Recalls
Warning Letters
Marketing
Special Reports
Fierce 50
Special Report
Awards Gala
Trending
Oncology
Supply Chain
AI and Machine Learning
Awards
Outsourcing Awards
Innovation Awards
Pharma Marketing Awards
Resources
Podcasts
Fierce Events
Industry Events
Webinars
Whitepapers
Survey
Events
Subscribe
Fierce Pharma
Fierce Biotech
Fierce Healthcare
Fierce Life Sciences Events
Advertise
About Us
rare diseases
Pharma
Zevra CEO drafts big ambitions for Miplyffa's US adoption curve
With Miplyffa, Zevra's CEO wants to transform the American treatment landscape for Niemann-Pick disease type C into one resembling Europe’s.
Fraiser Kansteiner
Jun 3, 2026 11:17am
FDA posts untitled letter for emails with eye-catching graphics
Jun 3, 2026 4:22am
PharmaEssentia taps Incyte alum as it eyes Besremi expansion
May 28, 2026 8:08am
Tyra creates awareness day to shine light on a rare cancer
May 22, 2026 4:21am
Tavneos patient starts resume in Japan amid safety scrutiny
May 21, 2026 11:38am
BioMarin lays off staffers at recently-acquired Amicus
May 12, 2026 5:12pm
